gene therapy
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Alarmed By Recent Events, Scientists Speak Out Against DIY Gene Therapy
It seems hard to fathom that scientific progress has advanced to a point where it’s suddenly possible for people to undertake something as complicated as gene therapy outside the safety and confines of a well-funded lab, but it has. In just the past few months we’ve seen not one, but two examples of people pursuing…
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Gene Therapy Restores Seven-Year-Old Boy’s Skin In ‘Major Biomedical Triumph’
Junctional epidermolysis bullosa is the sort of rare disease you are probably lucky to have never heard of. An often lethal genetic condition, from infancy it plagues its victim with painful blisters all over the body that causes the skin to become extremely fragile.
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The FDA Is Considering A Landmark Approval Of Gene Therapy To Cure Blindness
Today, a US Food and Drug Administration review committee published a document signalling that a historic moment in medicine may be on the horizon. The committee found that an experimental gene therapy for a rare inherited form of blindness improves vision, at least in the short term. If approved, the technique would be the first…
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Biotech Firm Halts ‘Revolutionary’ Cancer Treatment After Patient Deaths
Following the deaths of five patients, Juno Therapeutics has decided to pull the plug on an experimental cancer treatment that boosts the power of a patient’s immune cells. The news comes just days after the company’s rival, Kite Pharma, announced its success with a similar method, showing there’s still hope for this potentially revolutionary gene…